• Betibeglogene autotemcel, sold under the brand name Zynteglo, is a gene therapy for the treatment for beta thalassemia. It was developed by Bluebird Bio...
    21 KB (1,463 words) - 07:11, 6 August 2024
  • company's only - in the European Union (EU) - approved drug is betibeglogene autotemcel (Zynteglo), which treats transfusion-dependent beta thalassemia...
    15 KB (1,408 words) - 21:01, 17 October 2024
  • Thumbnail for Beta thalassemia
    There are two approved forms of gene therapy for beta thalassemia. Betibeglogene autotemcel, sold under the brand name Zynteglo, is a gene therapy for the...
    35 KB (6,225 words) - 08:38, 21 March 2025
  • Thumbnail for Thalassemia
    There are two approved forms of gene therapy for beta thalassemia. Betibeglogene autotemcel, sold under the brand name Zynteglo, is a gene therapy for the...
    75 KB (7,679 words) - 18:35, 17 March 2025
  • and mortality 7%. The best results are with very young people. Betibeglogene autotemcel, sold under the brand name Zynteglo, is a gene therapy for the...
    41 KB (4,621 words) - 16:57, 13 January 2025
  • Thumbnail for Gene therapy
    making it the most expensive drug ever. In May, the EMA approved betibeglogene autotemcel (Zynteglo) for treating beta thalassemia for people twelve years...
    179 KB (18,436 words) - 06:46, 7 April 2025
  • RMAT designated drugs include the novel CAR-T therapy Kymriah and betibeglogene autotemcel for beta thalassemia. As of 31 March 2021, 62 requests for RMAT...
    29 KB (1,621 words) - 17:30, 19 February 2025
  • lymphoma Beremagene geperpavec (Vyjuvek): treatment of wounds. Betibeglogene autotemcel (Zynteglo): treatment for beta thalassemia Brexucabtagene autoleucel...
    11 KB (857 words) - 23:07, 7 March 2025
  • (INN) Betaxon betazole (INN) bethanechol (INN) betiatide (INN) betibeglogene autotemcel (USAN, INN) Betimol Betnesol Betnovate Betoptic Pilo Betoptic S...
    15 KB (631 words) - 06:34, 16 February 2025
  • B06AX01 Crizanlizumab B06AX02 Betibeglogene autotemcel B06AX03 Voxelotor B06AX04 Mitapivat B06AX05 Exagamglogene autotemcel "ATC (Anatomical Therapeutic...
    1,011 bytes (217 words) - 03:43, 23 December 2024
  • Thumbnail for Intracellular delivery
    arylsulfatase A (ARSA) gene (European approval granted 2020). Betibeglogene autotemcel (branded as Zynteglo) for the treatment of transfusion-dependent...
    78 KB (8,788 words) - 19:06, 6 August 2024