Miglustat, sold under the brand name Zavesca among others, is a medication used to treat type I Gaucher disease and Pompe disease. It was approved for...

Velaglucerase (approved in 2010) Taliglucerase alfa (Elelyso) (approved in 2012) Miglustat is a small molecule, orally available drug that was first approved for...

therapy. Bone marrow transplant has been tried for type B. In January 2009, miglustat (Zavesca) was authorized in the European Union for the treatment of progressive...

1% of patients. No clinical interaction studies have been conducted. Miglustat appears to increase the clearance of imiglucerase by 70%, resulting in...

treatment for Niemann-Pick Disease, Type C Arimoclomol, in combination with miglustat, is indicated for the treatment of neurological symptoms associated with...

alfa, sold under the brand name Pombiliti, and used in combination with miglustat, is a medication used for the treatment of glycogen storage disease type...

multiple sclerosis, and migraine. One drug that has been tried is Miglustat. Miglustat is a glucosylceramide synthase inhibitor, which inhibits the synthesis...

a drug against type 2 diabetes. Miglustat is an iminosugar in which the ring oxygen is replaced by nitrogen. Miglustat a drug used to treat some rare lysosomal...

Another metabolic therapy under investigation for Tay–Sachs disease uses miglustat. This drug is a reversible inhibitor of the enzyme glucosylceramide synthase...

metabolized and is excreted by the kidneys. Alpha-glucosidase inhibitor Miglustat Voglibose "Migliotl: MedlinePlus Drug Information". MedlinePlus. National...

two-component therapy of Pombiliti (cipaglucosidase alfa-atga) and Opfolda (miglustat) 65 mg capsules for adults living with late-onset Pompe disease weighing...

medicines, N-hydroxyethyl-DNJ (miglitol) for diabetes and N-butyl-DNJ (miglustat) for Gaucher's disease. Anti-cancer and anti-viral activity was subsequently...

C enzyme, are still in development as potential male contraceptives. Miglustat (Zavesca or NB-DNJ) is a drug approved for treatment of several rare lipid...

mild disease-related neurological symptoms. Participants could receive miglustat, an enzyme inhibitor, as background treatment in the study. The US Food...

Sodium phenylbutyrate A16AX04 Nitisinone A16AX05 Zinc acetate A16AX06 Miglustat A16AX07 Sapropterin A16AX08 Teduglutide A16AX09 Glycerol phenylbutyrate...

effective in treating lysosomal diseases. She managed to get the drug (Miglustat) approved by the European Medicines Agency and Food and Drug Administration...

treat desmoid tumors Pombiliti To treat late-onset Pompe disease with miglustat Rivfloza To lower urinary oxalate levels in primary hyperoxaluria type...

receptor antagonist, see also: Endothelin receptor antagonist. Zavesca (miglustat): is currently the only approved oral treatment for patients with mild...

February 2018 the FDA accepted it and promised a response by August 2018. Miglustat, a drug for the treatment of Gaucher disease, with a similar structure...

β-glucocerebrosidase for enzyme replacement therapy of Gaucher's disease Miglustat, another orphan drug for the treatment of Gaucher's disease with a different...

include treatment with the drug OGT 918 (Zavesca). Gaucher's disease. Miglustat and eliglustat are substrate reduction therapies for Gaucher's disease...